Health technology appraisal of innovative therapies for Osteogenesis imperfecta: bridging clinical evidence to improve care for people living with rare disease (HERO)
Grant Data
Project Title
Health technology appraisal of innovative therapies for Osteogenesis imperfecta: bridging clinical evidence to improve care for people living with rare disease (HERO)
Principal Investigator
Professor Li, Xue
(Principal Investigator (PI))
Co-Investigator(s)
Professor To Michael Kai Tsun
(Co-Investigator)
Professor Cheung Ching Lung
(Co-Investigator)
Duration
24
Start Date
2024-05-16
Amount
927300
Conference Title
Health technology appraisal of innovative therapies for Osteogenesis imperfecta: bridging clinical evidence to improve care for people living with rare disease (HERO)
Keywords
Osteogenesis imperfecta, Health technology, Cutting-edge therapies, Cost-effectiveness
Discipline
Others - Medicine, Dentistry and Health
HKU Project Code
08220197
Grant Type
HMRF Research Fellowship Scheme 2022
Funding Year
2023
Status
On-going
Objectives
Osteogenesis imperfecta (OI) is a rare genetic disorder at birth and a lifelong condition causing considerable social-economic burden. Cutting-edge therapies are emerging under trial settings. We aim to conduct a health technology assessment (HTA) to understand the clinical efficacy, safety and cost-effectiveness of innovative medicines of OI for early health system preparedness of breakthrough therapies for rare diseases. No specific hypothesis will be tested.