Article: Population differences in the polyalanine domain and 6 new mutations in HLXB9 in patients with Currarino syndrome
| Title | Population differences in the polyalanine domain and 6 new mutations in HLXB9 in patients with Currarino syndrome |
|---|---|
| Authors | GarciaBarceló, M3 So, MT3 Lau, DKC3 Leon, TYY3 Yuan, ZW1 3 Cai, WS1 3 Lui, VCH3 Fu, M3 5 Herbrick, JA9 Gutter, E4 Proud, V4 Li, L5 PierreLouis, J7 Aleck, K2 Van Heurn, E8 Belloni, E6 Scherer, SW9 Tam, PKH3 |
| Issue Date | 2006 |
| Publisher | American Association for Clinical Chemistry, Inc. The Journal's web site is located at http://www.clinchem.org |
| Citation | Clinical Chemistry, 2006, v. 52 n. 1, p. 46-52 [How to Cite?] DOI: http://dx.doi.org/10.1373/clinchem.2005.056192 |
| Abstract | Background: The combination of partial absence of the sacrum, anorectal anomalies, and presacral mass constitutes Currarino syndrome (CS), which is associated with mutations in HLXB9. Methods: We analyzed 5 CS families and 6 sporadic cases for HLXB9 mutations by direct sequencing. Potentially pathologic expansions of HLXB9 GCC repeats were analyzed in patients, 4 general populations [Chinese, Japanese, Yoruba, and Centre du Etude Polymorphisme Human (CEPH)] from the HapMap project, and 145 healthy Chinese. Results: We identified 6 novel mutations affecting highly conserved residues (Serl85X, Trp215X, Ala26fs, Ala75/s, Met1Ile, and Arg273Cys). GCC allele and genotype distributions showed marked statistically significant differences. (GCC) 11 was the most common allele overall; its frequency ranged from 90% in CEPH to 68% in Yoruba and 50% in Chinese and Japanese populations. (GCC) 9 was almost as common as (GCC) 11 in Chinese and Japanese populations, whereas its frequency was <10% in Yoruba and CEPH populations. The Yoruba population had the highest frequency of the largest alleles [(GCC) 12 and (GCC) 13], which were almost absent in the other groups. Conclusions: Lack of HLXB9 mutations in some patients and the presence of variable phenotypes suggest DNA alterations in HLXB9 noncoding regions and/or in other genes encoding HLXB9 regulatory molecules or protein partners. If HLXB9, like other homeobox genes, has a threshold beyond which triplet expansions are pathologic, those populations enriched with larger alleles would be at a higher risk. The data illustrate the importance of ethnicity adjustment if these polymorphic markers are to be used in association studies. © 2006 American Association for Clinical Chemistry. |
| ISSN | 0009-9147 2011 Impact Factor: 7.905 2011 SCImago Journal Rankings: 0.650 |
| DOI | http://dx.doi.org/10.1373/clinchem.2005.056192 |
| ISI Accession Number ID | WOS:000234338800007 |
| References | References in Scopus |
| dc.contributor.author | GarciaBarceló, M |
|---|---|
| dc.contributor.author | So, MT |
| dc.contributor.author | Lau, DKC |
| dc.contributor.author | Leon, TYY |
| dc.contributor.author | Yuan, ZW |
| dc.contributor.author | Cai, WS |
| dc.contributor.author | Lui, VCH |
| dc.contributor.author | Fu, M |
| dc.contributor.author | Herbrick, JA |
| dc.contributor.author | Gutter, E |
| dc.contributor.author | Proud, V |
| dc.contributor.author | Li, L |
| dc.contributor.author | PierreLouis, J |
| dc.contributor.author | Aleck, K |
| dc.contributor.author | Van Heurn, E |
| dc.contributor.author | Belloni, E |
| dc.contributor.author | Scherer, SW |
| dc.contributor.author | Tam, PKH |
| dc.date.accessioned | 2010-09-06T08:40:28Z |
| dc.date.available | 2010-09-06T08:40:28Z |
| dc.date.issued | 2006 |
| dc.description.abstract | Background: The combination of partial absence of the sacrum, anorectal anomalies, and presacral mass constitutes Currarino syndrome (CS), which is associated with mutations in HLXB9. Methods: We analyzed 5 CS families and 6 sporadic cases for HLXB9 mutations by direct sequencing. Potentially pathologic expansions of HLXB9 GCC repeats were analyzed in patients, 4 general populations [Chinese, Japanese, Yoruba, and Centre du Etude Polymorphisme Human (CEPH)] from the HapMap project, and 145 healthy Chinese. Results: We identified 6 novel mutations affecting highly conserved residues (Serl85X, Trp215X, Ala26fs, Ala75/s, Met1Ile, and Arg273Cys). GCC allele and genotype distributions showed marked statistically significant differences. (GCC) 11 was the most common allele overall; its frequency ranged from 90% in CEPH to 68% in Yoruba and 50% in Chinese and Japanese populations. (GCC) 9 was almost as common as (GCC) 11 in Chinese and Japanese populations, whereas its frequency was <10% in Yoruba and CEPH populations. The Yoruba population had the highest frequency of the largest alleles [(GCC) 12 and (GCC) 13], which were almost absent in the other groups. Conclusions: Lack of HLXB9 mutations in some patients and the presence of variable phenotypes suggest DNA alterations in HLXB9 noncoding regions and/or in other genes encoding HLXB9 regulatory molecules or protein partners. If HLXB9, like other homeobox genes, has a threshold beyond which triplet expansions are pathologic, those populations enriched with larger alleles would be at a higher risk. The data illustrate the importance of ethnicity adjustment if these polymorphic markers are to be used in association studies. © 2006 American Association for Clinical Chemistry. |
| dc.description.nature | link_to_subscribed_fulltext |
| dc.identifier.citation | Clinical Chemistry, 2006, v. 52 n. 1, p. 46-52 [How to Cite?] DOI: http://dx.doi.org/10.1373/clinchem.2005.056192 |
| dc.identifier.doi | http://dx.doi.org/10.1373/clinchem.2005.056192 |
| dc.identifier.epage | 52 |
| dc.identifier.hkuros | 112900 |
| dc.identifier.isi | WOS:000234338800007 |
| dc.identifier.issn | 0009-9147 2011 Impact Factor: 7.905 2011 SCImago Journal Rankings: 0.650 |
| dc.identifier.issue | 1 |
| dc.identifier.openurl | ![]() |
| dc.identifier.pmid | 16254195 |
| dc.identifier.scopus | eid_2-s2.0-29744438814 |
| dc.identifier.spage | 46 |
| dc.identifier.uri | http://hdl.handle.net/10722/83391 |
| dc.identifier.volume | 52 |
| dc.language | eng |
| dc.publisher | American Association for Clinical Chemistry, Inc. The Journal's web site is located at http://www.clinchem.org |
| dc.publisher.place | United States |
| dc.relation.ispartof | Clinical Chemistry |
| dc.relation.references | References in Scopus |
| dc.title | Population differences in the polyalanine domain and 6 new mutations in HLXB9 in patients with Currarino syndrome |
| dc.type | Article |
Author Affiliations
- China Medical University Shenyang
- St. Joseph's Hospital and Medical Center
- The University of Hong Kong
- Children's Hospital of The King's Daughters Health System
- Beijing Children's Hospital
- Istituto Europeo di Oncologia
- University of Toronto
- University Hospital Maastricht
- Hospital for Sick Children, Toronto


