Article: Mutations in a gene encoding a novel protein tyrosine phosphatase cause progressive myoclonus epilepsy
| Title | Mutations in a gene encoding a novel protein tyrosine phosphatase cause progressive myoclonus epilepsy |
|---|---|
| Authors | Minassian, BA7 9 Lee Jeffrey, R7 Herbrick, JA7 Huizenga, J7 Soder, S7 Mungall, AJ3 Dunham, I3 Gardner, R1 Fong, CYG2 Carpenter, S7 Jardim, L6 Satishchandra, P4 Andermann, E8 Carter Snead III, O9 LopesCendes, I5 8 Tsui, LC7 DelgadoEscueta, AV2 Rouleau, GA5 8 Scherer, SW7 |
| Issue Date | 1998 |
| Publisher | Nature Publishing Group. The Journal's web site is located at http://www.genetics.nature.com |
| Citation | Nature Genetics, 1998, v. 20 n. 2, p. 171-174 [How to Cite?] DOI: http://dx.doi.org/10.1038/2470 |
| Abstract | Lafora's disease (LD; OMIM 254780) is an autosomal recessive form of progressive myoclonus epilepsy characterized by seizures and cumulative neurological deterioration. Onset occurs during late childhood and usually results in death within ten years of the first symptoms1,2. With few exceptions, patients follow a homogeneous clinical course despite the existence of genetic heterogeneity3. Biopsy of various tissues, including brain, revealed characteristic polyglucosan inclusions called Lafora bodies4-8, which suggested LD might be a generalized storage disease6,9. Using a positional cloning approach, we have identified at chromosome 6q24 a novel gene, EPM2A, that encodes a protein with consensus amino acid sequence indicative of a protein tyrosine phosphatase (PTP). mRNA transcripts representing alternatively spliced forms of EPM2A were found in every tissue examined, including brain. Six distinct DNA sequence variations in EPM2A in nine families, and one homozygous microdeletion in another family, have been found to cosegregate with LD. These mutations are predicted to cause deleterious effects in the putative protein product, named laforin, resulting in LD. |
| ISSN | 1061-4036 2011 Impact Factor: 35.532 2011 SCImago Journal Rankings: 8.923 |
| DOI | http://dx.doi.org/10.1038/2470 |
| ISI Accession Number ID | WOS:000076231300019 |
| References | References in Scopus |
| dc.contributor.author | Minassian, BA |
|---|---|
| dc.contributor.author | Lee Jeffrey, R |
| dc.contributor.author | Herbrick, JA |
| dc.contributor.author | Huizenga, J |
| dc.contributor.author | Soder, S |
| dc.contributor.author | Mungall, AJ |
| dc.contributor.author | Dunham, I |
| dc.contributor.author | Gardner, R |
| dc.contributor.author | Fong, CYG |
| dc.contributor.author | Carpenter, S |
| dc.contributor.author | Jardim, L |
| dc.contributor.author | Satishchandra, P |
| dc.contributor.author | Andermann, E |
| dc.contributor.author | Carter Snead III, O |
| dc.contributor.author | LopesCendes, I |
| dc.contributor.author | Tsui, LC |
| dc.contributor.author | DelgadoEscueta, AV |
| dc.contributor.author | Rouleau, GA |
| dc.contributor.author | Scherer, SW |
| dc.date.accessioned | 2007-09-12T03:51:47Z |
| dc.date.available | 2007-09-12T03:51:47Z |
| dc.date.issued | 1998 |
| dc.description.abstract | Lafora's disease (LD; OMIM 254780) is an autosomal recessive form of progressive myoclonus epilepsy characterized by seizures and cumulative neurological deterioration. Onset occurs during late childhood and usually results in death within ten years of the first symptoms1,2. With few exceptions, patients follow a homogeneous clinical course despite the existence of genetic heterogeneity3. Biopsy of various tissues, including brain, revealed characteristic polyglucosan inclusions called Lafora bodies4-8, which suggested LD might be a generalized storage disease6,9. Using a positional cloning approach, we have identified at chromosome 6q24 a novel gene, EPM2A, that encodes a protein with consensus amino acid sequence indicative of a protein tyrosine phosphatase (PTP). mRNA transcripts representing alternatively spliced forms of EPM2A were found in every tissue examined, including brain. Six distinct DNA sequence variations in EPM2A in nine families, and one homozygous microdeletion in another family, have been found to cosegregate with LD. These mutations are predicted to cause deleterious effects in the putative protein product, named laforin, resulting in LD. |
| dc.description.nature | abstract |
| dc.identifier.citation | Nature Genetics, 1998, v. 20 n. 2, p. 171-174 [How to Cite?] DOI: http://dx.doi.org/10.1038/2470 |
| dc.identifier.citeulike | 3892052 |
| dc.identifier.doi | http://dx.doi.org/10.1038/2470 |
| dc.identifier.epage | 174 |
| dc.identifier.isi | WOS:000076231300019 |
| dc.identifier.issn | 1061-4036 2011 Impact Factor: 35.532 2011 SCImago Journal Rankings: 8.923 |
| dc.identifier.issue | 2 |
| dc.identifier.openurl | ![]() |
| dc.identifier.pmid | 9771710 |
| dc.identifier.scopus | eid_2-s2.0-17344362307 |
| dc.identifier.spage | 171 |
| dc.identifier.uri | http://hdl.handle.net/10722/44343 |
| dc.identifier.volume | 20 |
| dc.language | eng |
| dc.publisher | Nature Publishing Group. The Journal's web site is located at http://www.genetics.nature.com |
| dc.publisher.place | United States |
| dc.relation.ispartof | Nature Genetics |
| dc.relation.references | References in Scopus |
| dc.subject.mesh | Chromosomes, human, pair 6 |
| dc.subject.mesh | Epilepsies, myoclonic - enzymology - genetics |
| dc.subject.mesh | Mutation |
| dc.subject.mesh | Protein-tyrosine-phosphatase - genetics |
| dc.subject.mesh | Rna, messenger - metabolism |
| dc.title | Mutations in a gene encoding a novel protein tyrosine phosphatase cause progressive myoclonus epilepsy |
| dc.type | Article |
Author Affiliations
- Salisbury District Hospital
- David Geffen School of Medicine at UCLA
- Wellcome Trust Sanger Institute
- National Institute of Mental Health and Neuro Sciences
- Montreal General Hospital
- Hospital de Clinicas de Porto Alegre
- University of Toronto
- McGill University
- Hospital for Sick Children, Toronto


