Article: Genome-wide copy number analysis uncovers a new HSCR gene: NRG3
| Title | Genome-wide copy number analysis uncovers a new HSCR gene: NRG3 |
|---|---|
| Authors | Tang, CSM1 Cheng, G1 So, MT1 Yip, BHK1 Miao, XP1 5 Wong, EHM1 Ngan, ESW1 Lui, VCH1 Song, YQ1 Chan, D1 Cheung, K1 Yuan, ZW4 Lei, L3 Chung, PHY1 Liu, XL1 Wong, KKY1 Marshall, CR2 Scherer, S2 6 Cherny, SS1 Sham, PC1 Tam, PKH1 GarciaBarceló, MM1 |
| Keywords | Copy number variation Gene deletion Gene duplication Gene expression regulation Gene frequency |
| Issue Date | 2012 |
| Publisher | Public Library of Science. The Journal's web site is located at http://www.plosgenetics.org/ |
| Citation | Plos Genetics, 2012, v. 8 n. 5 [How to Cite?] DOI: http://dx.doi.org/10.1371/journal.pgen.1002687 |
| Abstract | Hirschsprung disease (HSCR) is a congenital disorder characterized by aganglionosis of the distal intestine. To assess the contribution of copy number variants (CNVs) to HSCR, we analysed the data generated from our previous genome-wide association study on HSCR patients, whereby we identified NRG1 as a new HSCR susceptibility locus. Analysis of 129 Chinese patients and 331 ethnically matched controls showed that HSCR patients have a greater burden of rare CNVs (p = 1.50×10 -5), particularly for those encompassing genes (p = 5.00×10 -6). Our study identified 246 rare-genic CNVs exclusive to patients. Among those, we detected a NRG3 deletion (p = 1.64×10 -3). Subsequent follow-up (96 additional patients and 220 controls) on NRG3 revealed 9 deletions (combined p = 3.36×10 -5) and 2 de novo duplications among patients and two deletions among controls. Importantly, NRG3 is a paralog of NRG1. Stratification of patients by presence/absence of HSCR-associated syndromes showed that while syndromic-HSCR patients carried significantly longer CNVs than the non-syndromic or controls (p = 1.50×10 -5), non-syndromic patients were enriched in CNV number when compared to controls (p = 4.00×10 -6) or the syndromic counterpart. Our results suggest a role for NRG3 in HSCR etiology and provide insights into the relative contribution of structural variants in both syndromic and non-syndromic HSCR. This would be the first genome-wide catalog of copy number variants identified in HSCR. © 2012 Tang et al. |
| ISSN | 1553-7390 2011 Impact Factor: 8.694 2011 SCImago Journal Rankings: 1.813 |
| DOI | http://dx.doi.org/10.1371/journal.pgen.1002687 |
| PubMed Central ID | PMC3349728 |
| References | References in Scopus |
| Grants | Exon sequencing of Semaphorin, a novel Hirschsprung's Disease susceptibility locus Identification of functional variants in Neuregulin-1 (NRG1), a newly discovered Hirschsprungs disease gene Genetic dissection of Hirschsprung's disease Functional characterization of the V226L, H347Y, and P356L NRG1 mutations identified in Hirschsprung's disease patients Sequencing of the neuregulin-1 (NRG1) gene in Hisrchprung's disease patients Developmental genomics and skeletal research |
| dc.contributor.author | Tang, CSM | ||||||||||
|---|---|---|---|---|---|---|---|---|---|---|---|
| dc.contributor.author | Cheng, G | ||||||||||
| dc.contributor.author | So, MT | ||||||||||
| dc.contributor.author | Yip, BHK | ||||||||||
| dc.contributor.author | Miao, XP | ||||||||||
| dc.contributor.author | Wong, EHM | ||||||||||
| dc.contributor.author | Ngan, ESW | ||||||||||
| dc.contributor.author | Lui, VCH | ||||||||||
| dc.contributor.author | Song, YQ | ||||||||||
| dc.contributor.author | Chan, D | ||||||||||
| dc.contributor.author | Cheung, K | ||||||||||
| dc.contributor.author | Yuan, ZW | ||||||||||
| dc.contributor.author | Lei, L | ||||||||||
| dc.contributor.author | Chung, PHY | ||||||||||
| dc.contributor.author | Liu, XL | ||||||||||
| dc.contributor.author | Wong, KKY | ||||||||||
| dc.contributor.author | Marshall, CR | ||||||||||
| dc.contributor.author | Scherer, S | ||||||||||
| dc.contributor.author | Cherny, SS | ||||||||||
| dc.contributor.author | Sham, PC | ||||||||||
| dc.contributor.author | Tam, PKH | ||||||||||
| dc.contributor.author | GarciaBarceló, MM | ||||||||||
| dc.date.accessioned | 2012-06-22T06:19:38Z | ||||||||||
| dc.date.available | 2012-06-22T06:19:38Z | ||||||||||
| dc.date.issued | 2012 | ||||||||||
| dc.description.abstract | Hirschsprung disease (HSCR) is a congenital disorder characterized by aganglionosis of the distal intestine. To assess the contribution of copy number variants (CNVs) to HSCR, we analysed the data generated from our previous genome-wide association study on HSCR patients, whereby we identified NRG1 as a new HSCR susceptibility locus. Analysis of 129 Chinese patients and 331 ethnically matched controls showed that HSCR patients have a greater burden of rare CNVs (p = 1.50×10 -5), particularly for those encompassing genes (p = 5.00×10 -6). Our study identified 246 rare-genic CNVs exclusive to patients. Among those, we detected a NRG3 deletion (p = 1.64×10 -3). Subsequent follow-up (96 additional patients and 220 controls) on NRG3 revealed 9 deletions (combined p = 3.36×10 -5) and 2 de novo duplications among patients and two deletions among controls. Importantly, NRG3 is a paralog of NRG1. Stratification of patients by presence/absence of HSCR-associated syndromes showed that while syndromic-HSCR patients carried significantly longer CNVs than the non-syndromic or controls (p = 1.50×10 -5), non-syndromic patients were enriched in CNV number when compared to controls (p = 4.00×10 -6) or the syndromic counterpart. Our results suggest a role for NRG3 in HSCR etiology and provide insights into the relative contribution of structural variants in both syndromic and non-syndromic HSCR. This would be the first genome-wide catalog of copy number variants identified in HSCR. © 2012 Tang et al. | ||||||||||
| dc.description.grant | Exon sequencing of Semaphorin, a novel Hirschsprung's Disease susceptibility locus | ||||||||||
| dc.description.grant | Identification of functional variants in Neuregulin-1 (NRG1), a newly discovered Hirschsprungs disease gene | ||||||||||
| dc.description.grant | Genetic dissection of Hirschsprung's disease | ||||||||||
| dc.description.grant | Functional characterization of the V226L, H347Y, and P356L NRG1 mutations identified in Hirschsprung's disease patients | ||||||||||
| dc.description.grant | Sequencing of the neuregulin-1 (NRG1) gene in Hisrchprung's disease patients | ||||||||||
| dc.description.grant | Developmental genomics and skeletal research | ||||||||||
| dc.description.grantcode | 101808 | ||||||||||
| dc.description.grantcode | 100485 | ||||||||||
| dc.description.grantcode | 96945 | ||||||||||
| dc.description.grantcode | 101813 | ||||||||||
| dc.description.grantcode | 99882 | ||||||||||
| dc.description.grantcode | 44444 | ||||||||||
| dc.description.nature | published_or_final_version | ||||||||||
| dc.identifier.citation | Plos Genetics, 2012, v. 8 n. 5 [How to Cite?] DOI: http://dx.doi.org/10.1371/journal.pgen.1002687 | ||||||||||
| dc.identifier.doi | http://dx.doi.org/10.1371/journal.pgen.1002687 | ||||||||||
| dc.identifier.hkuros | 200158 | ||||||||||
| dc.identifier.isi | WOS:000304864000018
Funding Information: This work was supported by the Hong Kong Research Grants Council (HKU 775907M to PK-HT and HKU 765609M to M-MG-B) and by the Seed Funding Programme for Basic Research (200910159040 and 200811159006 to M-MG-B and 200911159190 to SSC). Support was also received from the University Grants Committee of Hong Kong (AoE/M-04/04) and AOSPINE (AOSBRC-07-02 to DC). The funders had no role in study design, data collection and analysis, decision to publish, or preparation of the manuscript. | ||||||||||
| dc.identifier.issn | 1553-7390 2011 Impact Factor: 8.694 2011 SCImago Journal Rankings: 1.813 | ||||||||||
| dc.identifier.issue | 5 | ||||||||||
| dc.identifier.openurl | ![]() | ||||||||||
| dc.identifier.pmcid | PMC3349728 | ||||||||||
| dc.identifier.pmid | 22589734 | ||||||||||
| dc.identifier.scopus | eid_2-s2.0-84863680217 | ||||||||||
| dc.identifier.uri | http://hdl.handle.net/10722/149062 | ||||||||||
| dc.identifier.volume | 8 | ||||||||||
| dc.language | eng | ||||||||||
| dc.publisher | Public Library of Science. The Journal's web site is located at http://www.plosgenetics.org/ | ||||||||||
| dc.publisher.place | United States | ||||||||||
| dc.relation.ispartof | PLoS Genetics | ||||||||||
| dc.relation.references | References in Scopus | ||||||||||
| dc.rights | Creative Commons: Attribution 3.0 Hong Kong License | ||||||||||
| dc.subject | Copy number variation | ||||||||||
| dc.subject | Gene deletion | ||||||||||
| dc.subject | Gene duplication | ||||||||||
| dc.subject | Gene expression regulation | ||||||||||
| dc.subject | Gene frequency | ||||||||||
| dc.title | Genome-wide copy number analysis uncovers a new HSCR gene: NRG3 | ||||||||||
| dc.type | Article |
Author Affiliations
- The University of Hong Kong Li Ka Shing Faculty of Medicine
- Hospital for Sick Children, The Centre for Applied Genomics, Toronto
- Shenzhen Children's Hospital
- China Medical University Shenyang
- Huazhong University of Science and Technology
- University of Toronto


