Article: Alleles at the Nicastrin locus modify presenilin 1-deficiency phenotype
| Title | Alleles at the Nicastrin locus modify presenilin 1-deficiency phenotype |
|---|---|
| Authors | Rozmahel, R2 4 5 Mount, HTJ2 3 Chen, F2 Nguyen, V2 5 Huang, J2 5 Erdebil, S2 Liauw, J2 Yu, G2 Hasegawa, H2 Gu, Y2 Song, YQ2 Schmidt, SD1 Nixon, RA2 3 Mathews, PM1 Bergeron, C2 3 Fraser, P2 Westaway, D2 St GeorgeHyslop, P2 3 |
| Issue Date | 2002 |
| Publisher | National Academy of Sciences. The Journal's web site is located at http://www.pnas.org |
| Citation | Proceedings Of The National Academy Of Sciences Of The United States Of America, 2002, v. 99 n. 22, p. 14452-14457 [How to Cite?] DOI: http://dx.doi.org/10.1073/pnas.222413999 |
| Abstract | Presenilin 1 (PS1), presenilin 2, and nicastrin form high molecular weight complexes that are necessary for the endoproteolysis of several type 1 transmembrane proteins, including amyloid precursor protein (APP) and the Notch receptor, by apparently similar mechanisms. The cleavage of the Notch receptor at the S3-site releases a C-terminal cytoplasmic fragment (Notch intracellular domain) that acts as the intracellular transduction molecule for Notch activation. Missense mutations in the presenilins cause familial Alzheimer's disease by augmenting the γ-secretase cleavage of APP and overproducing one of the proteolytic derivatives, the Aβ peptide. Null mutations in PS1 inhibit both γ-secretase cleavage of APP and S3-site cleavage of the Notch receptor. Mice lacking PS1 function have defective Notch signaling and die perinatally with severe skeletal and brain deformities. We report here that a genetic modifier on mouse distal chromosome 1, coinciding with the locus containing Nicastrin, influences presenilin-mediated Notch S3-site cleavage and the resultant Notch phenotype without affecting presenilin-mediated APP γ-site cleavage. Two missense substitutions of residues conserved among vertebrates have been identified in nicastrin. These results indicate that Notch S3-site cleavage and APP γ-site cleavage are distinct presenilin-dependent processes and support a functional interaction between nicastrin and presenilins in vertebrates. The dissociation of Notch S3-site and APP γ-site cleavage activities will facilitate development of γ-secretase inhibitors for treatment of Alzheimer's disease. |
| ISSN | 0027-8424 2011 Impact Factor: 9.681 2011 SCImago Journal Rankings: 1.754 |
| DOI | http://dx.doi.org/10.1073/pnas.222413999 |
| PubMed Central ID | PMC137904 |
| References | References in Scopus |
| dc.contributor.author | Rozmahel, R |
|---|---|
| dc.contributor.author | Mount, HTJ |
| dc.contributor.author | Chen, F |
| dc.contributor.author | Nguyen, V |
| dc.contributor.author | Huang, J |
| dc.contributor.author | Erdebil, S |
| dc.contributor.author | Liauw, J |
| dc.contributor.author | Yu, G |
| dc.contributor.author | Hasegawa, H |
| dc.contributor.author | Gu, Y |
| dc.contributor.author | Song, YQ |
| dc.contributor.author | Schmidt, SD |
| dc.contributor.author | Nixon, RA |
| dc.contributor.author | Mathews, PM |
| dc.contributor.author | Bergeron, C |
| dc.contributor.author | Fraser, P |
| dc.contributor.author | Westaway, D |
| dc.contributor.author | St GeorgeHyslop, P |
| dc.date.accessioned | 2011-07-14T07:03:08Z |
| dc.date.available | 2011-07-14T07:03:08Z |
| dc.date.issued | 2002 |
| dc.description.abstract | Presenilin 1 (PS1), presenilin 2, and nicastrin form high molecular weight complexes that are necessary for the endoproteolysis of several type 1 transmembrane proteins, including amyloid precursor protein (APP) and the Notch receptor, by apparently similar mechanisms. The cleavage of the Notch receptor at the S3-site releases a C-terminal cytoplasmic fragment (Notch intracellular domain) that acts as the intracellular transduction molecule for Notch activation. Missense mutations in the presenilins cause familial Alzheimer's disease by augmenting the γ-secretase cleavage of APP and overproducing one of the proteolytic derivatives, the Aβ peptide. Null mutations in PS1 inhibit both γ-secretase cleavage of APP and S3-site cleavage of the Notch receptor. Mice lacking PS1 function have defective Notch signaling and die perinatally with severe skeletal and brain deformities. We report here that a genetic modifier on mouse distal chromosome 1, coinciding with the locus containing Nicastrin, influences presenilin-mediated Notch S3-site cleavage and the resultant Notch phenotype without affecting presenilin-mediated APP γ-site cleavage. Two missense substitutions of residues conserved among vertebrates have been identified in nicastrin. These results indicate that Notch S3-site cleavage and APP γ-site cleavage are distinct presenilin-dependent processes and support a functional interaction between nicastrin and presenilins in vertebrates. The dissociation of Notch S3-site and APP γ-site cleavage activities will facilitate development of γ-secretase inhibitors for treatment of Alzheimer's disease. |
| dc.description.nature | Link_to_subscribed_fulltext |
| dc.identifier.citation | Proceedings Of The National Academy Of Sciences Of The United States Of America, 2002, v. 99 n. 22, p. 14452-14457 [How to Cite?] DOI: http://dx.doi.org/10.1073/pnas.222413999 |
| dc.identifier.doi | http://dx.doi.org/10.1073/pnas.222413999 |
| dc.identifier.epage | 14457 |
| dc.identifier.isi | WOS:000178967400087 |
| dc.identifier.issn | 0027-8424 2011 Impact Factor: 9.681 2011 SCImago Journal Rankings: 1.754 |
| dc.identifier.issue | 22 |
| dc.identifier.pmcid | PMC137904 |
| dc.identifier.pmid | 12388777 |
| dc.identifier.scopus | eid_2-s2.0-0037195102 |
| dc.identifier.spage | 14452 |
| dc.identifier.uri | http://hdl.handle.net/10722/134767 |
| dc.identifier.volume | 99 |
| dc.publisher | National Academy of Sciences. The Journal's web site is located at http://www.pnas.org |
| dc.publisher.place | United States |
| dc.relation.ispartof | Proceedings of the National Academy of Sciences of the United States of America |
| dc.relation.references | References in Scopus |
| dc.subject.mesh | *Alleles |
| dc.subject.mesh | Amyloid Precursor Protein Secretases |
| dc.subject.mesh | Amyloid beta-Peptides/metabolism |
| dc.subject.mesh | Amyloid beta-Protein Precursor/metabolism |
| dc.subject.mesh | Animals |
| dc.subject.mesh | Aspartic Acid Endopeptidases |
| dc.subject.mesh | Binding Sites |
| dc.subject.mesh | Breeding |
| dc.subject.mesh | Chromosome Mapping |
| dc.subject.mesh | Endopeptidases/metabolism |
| dc.subject.mesh | Female |
| dc.subject.mesh | Male |
| dc.subject.mesh | Membrane Glycoproteins/*genetics |
| dc.subject.mesh | Membrane Proteins/genetics/*metabolism |
| dc.subject.mesh | Mice |
| dc.subject.mesh | Mice, Inbred C57BL |
| dc.subject.mesh | Mice, Knockout |
| dc.subject.mesh | Peptide Fragments/metabolism |
| dc.subject.mesh | Phenotype |
| dc.subject.mesh | Presenilin-1 |
| dc.subject.mesh | Receptors, Notch |
| dc.subject.mesh | Spine/*abnormalities |
| dc.title | Alleles at the Nicastrin locus modify presenilin 1-deficiency phenotype |
| dc.type | Article |
Author Affiliations
- New York University Langone Medical Center
- University of Toronto
- Queens Health Network
- University of Alabama
- Hospital for Sick Children, Toronto

