Article: Mutational analysis of SHH and GLI3 in anorectal malformations
| Title | Mutational analysis of SHH and GLI3 in anorectal malformations |
|---|---|
| Authors | GarciaBarceló, MM4 Lui, VCH4 Miao, X4 So, MT4 Leon, TYY4 Yuan, ZW3 Li, L7 Liu, L2 Wang, B2 Sun, XB8 Huang, LM6 Tou, JF5 Ngan, ESW4 Cherny, SS1 4 Chan, KW9 Lee, KH9 Wang, W3 Wong, KKY4 Tam, PKH4 |
| Keywords | Anorectal malformations GLI3 SHH |
| Issue Date | 2008 |
| Publisher | John Wiley & Sons, Inc. The Journal's web site is located at http://www3.interscience.wiley.com/cgi-bin/jhome/102526943 |
| Citation | Birth Defects Research Part A - Clinical And Molecular Teratology, 2008, v. 82 n. 9, p. 644-648 [How to Cite?] DOI: http://dx.doi.org/10.1002/bdra.20482 |
| Abstract | BACKGROUND: Anorectal malformations (congenital absence of the anal opening) are among the most common pediatric surgical problems and carry a significant chronic morbidity. METHODS: Direct sequencing was used to screen 88 anorectal malformations patients for mutations and polymorphisms in SHH and GLI3. These genes were chosen according to the phenotype presented by mutant mice and their expression patterns. RESULTS: We report on 10 GLI3 variants (IVS3+141C>G, T183A, IVS4+124T>C, IVS7+17G>A, IVS8+1 G>C, N503N, P941P, P998L, A1005A, A1039A) and four SHH mutation/variants (IVS1-49C>T, IVS2+111A>C, L214L, G290D). CONCLUSIONS: These variants are not over-represented in the healthy population and most are predicted to be benign. This study conveys the problematic assessment of the pathogenic role in disease of rare point mutations and variants. © 2008 Wiley-Liss, Inc. |
| ISSN | 1542-0752 2011 SCImago Journal Rankings: 0.199 |
| DOI | http://dx.doi.org/10.1002/bdra.20482 |
| ISI Accession Number ID | WOS:000259713600006 |
| References | References in Scopus |
| dc.contributor.author | GarciaBarceló, MM |
|---|---|
| dc.contributor.author | Lui, VCH |
| dc.contributor.author | Miao, X |
| dc.contributor.author | So, MT |
| dc.contributor.author | Leon, TYY |
| dc.contributor.author | Yuan, ZW |
| dc.contributor.author | Li, L |
| dc.contributor.author | Liu, L |
| dc.contributor.author | Wang, B |
| dc.contributor.author | Sun, XB |
| dc.contributor.author | Huang, LM |
| dc.contributor.author | Tou, JF |
| dc.contributor.author | Ngan, ESW |
| dc.contributor.author | Cherny, SS |
| dc.contributor.author | Chan, KW |
| dc.contributor.author | Lee, KH |
| dc.contributor.author | Wang, W |
| dc.contributor.author | Wong, KKY |
| dc.contributor.author | Tam, PKH |
| dc.date.accessioned | 2010-05-31T03:55:28Z |
| dc.date.available | 2010-05-31T03:55:28Z |
| dc.date.issued | 2008 |
| dc.description.abstract | BACKGROUND: Anorectal malformations (congenital absence of the anal opening) are among the most common pediatric surgical problems and carry a significant chronic morbidity. METHODS: Direct sequencing was used to screen 88 anorectal malformations patients for mutations and polymorphisms in SHH and GLI3. These genes were chosen according to the phenotype presented by mutant mice and their expression patterns. RESULTS: We report on 10 GLI3 variants (IVS3+141C>G, T183A, IVS4+124T>C, IVS7+17G>A, IVS8+1 G>C, N503N, P941P, P998L, A1005A, A1039A) and four SHH mutation/variants (IVS1-49C>T, IVS2+111A>C, L214L, G290D). CONCLUSIONS: These variants are not over-represented in the healthy population and most are predicted to be benign. This study conveys the problematic assessment of the pathogenic role in disease of rare point mutations and variants. © 2008 Wiley-Liss, Inc. |
| dc.description.nature | link_to_subscribed_fulltext |
| dc.identifier.citation | Birth Defects Research Part A - Clinical And Molecular Teratology, 2008, v. 82 n. 9, p. 644-648 [How to Cite?] DOI: http://dx.doi.org/10.1002/bdra.20482 |
| dc.identifier.doi | http://dx.doi.org/10.1002/bdra.20482 |
| dc.identifier.eissn | 1542-0760 |
| dc.identifier.epage | 648 |
| dc.identifier.hkuros | 152819 |
| dc.identifier.isi | WOS:000259713600006 |
| dc.identifier.issn | 1542-0752 2011 SCImago Journal Rankings: 0.199 |
| dc.identifier.issue | 9 |
| dc.identifier.pmid | 18655123 |
| dc.identifier.scopus | eid_2-s2.0-52249090865 |
| dc.identifier.spage | 644 |
| dc.identifier.uri | http://hdl.handle.net/10722/59691 |
| dc.identifier.volume | 82 |
| dc.language | eng |
| dc.publisher | John Wiley & Sons, Inc. The Journal's web site is located at http://www3.interscience.wiley.com/cgi-bin/jhome/102526943 |
| dc.publisher.place | United States |
| dc.relation.ispartof | Birth Defects Research Part A - Clinical and Molecular Teratology |
| dc.relation.references | References in Scopus |
| dc.subject | Anorectal malformations |
| dc.subject | GLI3 |
| dc.subject | SHH |
| dc.title | Mutational analysis of SHH and GLI3 in anorectal malformations |
| dc.type | Article |
Author Affiliations
- The University of Hong Kong Li Ka Shing Faculty of Medicine
- Shenzhen Children's Hospital
- China Medical University Shenyang
- The University of Hong Kong
- Zhejiang Children's Hospital
- Peking University
- Capital Institute of Pediatrics
- Shandong University School of Medicine
- Chinese University of Hong Kong

